Krystal Biotech Touts Positive KB407 CF Gene Therapy Data, Eyes Repeat Dosing and Registrational Path

Krystal Biotech (NASDAQ:KRYS) said it has generated positive interim clinical results for its inhaled cystic fibrosis (CF) ...

Krystal Biotech Announces Positive Interim Clinical Update from KB407 Phase 1 CORAL-1 Study with Confirmation of Wild-Type CFTR Delivery to the Lungs of Patients with Cystic ...

Confirmed wild-type CFTR delivery and expression in conducting airway cells of patients with class I mutationsKB407 transduction confirmed in all ...
Fierce Biotech

Baby KJ scientist launches personalized CRISPR therapy startup

Menlo Ventures has made a $16 million bet that the “ baby KJ ” custom CRISPR therapy success story is repeatable. The funding ...
BioPharma Dive

Aurora sets out to capitalize on FDA’s new framework for bespoke drug therapies

Co-founded by Jennifer Doudna and Fyodor Urnov, the company intends to simultaneously develop many gene editing treatments ...
Palm Beach Post

Can a pill thwart a brain gene mutation? A $7.7M grant helps a Jupiter institute find out

JUPITER — A research institution at the center of northern Palm Beach County's biotech industry has received a $7.7 million federal grant to develop medicine to help people with brain disorders. The ...