Researchers in the WashU Medicine Department of Ophthalmology & Visual Sciences have discovered key neuroprotective genes ...

A treatment that targets dysfunctional photoreceptors regardless of the underlying genetic mutation leads to improved ...

A novel gene therapy (ABBV-RGX-314) was well tolerated and reduced treatment burden in patients with bilateral neovascular age-related macular degeneration (AMD), according to results of a phase II ...

Researchers at Penn’s School of Veterinary Medicine have developed new mechanisms to treat advanced forms of inherited retinal degeneration, bridging a previous gap in patient treatments. Raghavi ...

Inherited retinal degeneration (IRD) encompasses various disorders characterized by progressive loss of retinal photoreceptor cells, ultimately leading to vision loss and blindness. Among the numerous ...

Target Enrollment Achieved with the Inclusion of Participants with Both Dominant and Recessive Forms of BEST DiseaseBaseline ...

GenSight Biologics (Euronext: SIGHT, ISIN: FR0013183985, PEA-PME eligible), a biopharma company focused on developing and commercializing innovative gene therapies for retinal neurodegenerative ...

Opus Genetics, Inc., a clinical-stage biotechnology company focusing on gene therapies for inherited retinal diseases, announced upcoming presentations at various scientific conferences in May 2025.

Advances in Vitreoretinal Disease Management Why Target Retinal Disease With Gene Therapy? Retinal Gene Therapy to Replace a Defective Gene Product: Early Results of Human Clinical Trials Expanding ...

Researchers at Johns Hopkins and their collaborators conducted an open-label phase I clinical trial of a new treatment, in which a viral vector expressing the gene for sFLT01, a protein that ...

"This pivotal work from the group at the University of Iowa has shown that one of the most severe degenerative diseases affecting the retina, juvenile NCL, may also be treatable with gene therapy." ...