For highly aggressive types of blood cancer, stem cell transplantation is often the only potentially curative therapy, yet ...

A Phase I/II clinical trial shows that a stem cell transplant that removes CD33 from donor cells using CRISPR can prevent ...

Stuart Orkin and Swee Lay Thein shared a Breakthrough Prize in Life Sciences for their research on genetic causes of sickle ...

Beta thalassemia major, also known as Cooley’s anemia and transfusion-dependent beta thalassemia, causes the body’s red blood ...

A first-of-its-kind trial is testing adult stem cell transplants for advanced dry macular degeneration. Early results show the treatment is safe and can significantly improve vision, even in severely ...

The first patient in Louisiana to receive genetically edited therapy for sickle cell disease went home this week after months in isolation at Manning Family Children's Hospital in New Orleans. Daniel ...

As blood stem cells age, their lysosomes become overactive and damaged, triggering inflammation and weakening the body’s ...

Years before he conducted the research that would earn him a Nobel Prize in Physiology and Medicine, Shinya Yamanaka, MD, Ph.D., was a postdoctoral scientist at Gladstone Institutes, studying genes.

Medical history has been made in Louisiana. On Tuesday, the first person in the state to receive gene therapy for sickle cell disease left the hospital after a six-week-long stay. The hope is that ...

Doctors have linked a boy's tumor to a gene therapy, but say the rare risks need to be weighed against the profound benefits ...

Data demonstrate distinct functional signatures across MSC-derived extracellular vesicles supporting targeted regenerative and aesthetic ...